Lipid therapy

Results: 50



#Item
21Rare diseases / Stem cells / Lipid storage disorders / NPC1 / Autophagy / Niemann–Pick disease / Induced pluripotent stem cell / Lysosome / Mammalian target of rapamycin / Biology / Chemistry / Cell biology

Combination therapy a potential strategy for treating Niemann Pick disease

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Source URL: medicalxpress.com

Language: English - Date: 2015-02-08 10:41:51
22Fabry disease / Medicine / Enzyme replacement therapy / Lysosomal storage disease / Fabry / Robert J. Desnick / Health / Rare diseases / Lipid storage disorders

Microsoft PowerPoint - Koning CORDMarch22009Final.ppt [Compatibility Mode]

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Source URL: www.raredisorders.ca

Language: English - Date: 2009-04-08 12:51:18
23Rare diseases / Medicine / Neuronal ceroid lipofuscinosis / Batten disease / Gene therapy / Health / Biology / Lipid storage disorders

Gene Therapy for LINCL CSF Amendment

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Source URL: osp.od.nih.gov

Language: English - Date: 2013-12-31 13:21:33
24Organ failure / Lipid storage disorders / Rare diseases / Fabry disease / Kidney diseases / Chronic kidney disease / Enzyme replacement therapy / Renal function / Lysosomal storage disease / Health / Anatomy / Medicine

Microsoft PowerPoint - Fabry Figures reworked bb.ppt

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Source URL: www.fabry.org

Language: English - Date: 2014-12-04 03:16:52
25Pediatrics / Lipid storage disorders / Medical genetics / Lysosomal storage disease / Newborn screening / Inborn error of metabolism / Genetic disorder / Cystic fibrosis / Enzyme replacement therapy / Health / Medicine / Rare diseases

Microsoft Word - Document1

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Source URL: www.hrsa.gov

Language: English - Date: 2014-12-04 01:13:21
26Lipid storage disorders / Rare diseases / Canavan disease / Leukodystrophies / Medical genetics / Bioethics / Gene therapy / N-Acetylaspartic acid / Canavan / Health / Biology / Medicine

http://archives.newstimeslive.com/view/story.php?id=10644&categ

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Source URL: www.canavan.org

Language: English - Date: 2009-11-06 14:10:04
27Lipid storage disorders / Rare diseases / Cellular processes / Lysosomal storage disease / Lysosome / Autophagy / Endosome / Mannose 6-phosphate / Substrate reduction therapy / Biology / Cell biology / Organelles

Research Presented 2008 Lysosomal Diseases and the Brain Conference Organized by the Children’s Gaucher Research Fund --- Speaker Abstracts --Molecular Mechanisms of Lysosome Biogenesis Juan S. Bonifacino, Ph.D. - juan

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Source URL: www.childrensgaucher.org

Language: English - Date: 2010-07-24 10:47:39
28Rare diseases / Leukodystrophies / Lipid storage disorders / Canavan disease / Medical genetics / Molecular biology / Paola Leone / Gene therapy / Myelin / Biology / Health / Medicine

http://archives.newstimeslive.com/view/story.php?id=7126&catego

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Source URL: www.canavan.org

Language: English - Date: 2009-11-06 14:09:58
29Rare diseases / Lipid storage disorders / Gene delivery / Emerging technologies / Molecular biology / Canavan disease / Gene therapy / Paola Leone / Virus / Biology / Health / Medicine

http://nl.newsbank.com/nl-search/we/Archives?p_action=doc&p_doc

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Source URL: www.canavan.org

Language: English - Date: 2009-11-06 14:10:26
30Gene delivery / Rare diseases / Lipid storage disorders / Leukodystrophies / Canavan disease / Emerging technologies / Paola Leone / Gene therapy / Myelin / Biology / Health / Medicine

Page 1 of 3 Sat, Sep. 17, 2005 Sending genes to save a child Pa. parents gamble on an unproven therapy to give their

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Source URL: www.canavan.org

Language: English - Date: 2009-11-06 14:10:29
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